Gene and Cell

Preclinical Evaluation of ADVM-062, a Novel Intravitreal Gene Therapy Vector for the Treatment of Blue Cone Monochromacy

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Molecular Therapy

Semiquantitative Methods for GFP Immunohistochemistry and In Situ Hybridization to Evaluate AAV Transduction of Mouse Retinal Cells Following Subretinal Injection

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Toxicologic Pathology, 49(3), pp.537-543

Ocular Safety of AAV2. 7m8-ChrimsonR-tdTomato (GS030-DP) following intravitreous injection and exposure to 595 nm LED light in blind rd1 mice

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Investigative Ophthalmology & Visual Science, 59(9), pp.5658-5658

Preliminary tolerability of iPSC-Derived RPE on PLGA scaffold implantation in RNU Nude Rats

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American Society of Gene & Cell Therapy Annual Meeting. Mol Ther; 25(5S1)

Cone-specific promoters for gene therapy of achromatopsia and other retinal diseases

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Human gene therapy, 27(1), pp.72-82

Functional and Structural Effects of Subretinal Dose Delivery in Mice

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Investigative Ophthalmology & Visual Science, 56(7), pp.245-245

Safety and biodistribution of an equine infectious anemia-based gene therapy, Retinostat®, for age-related macular degeneration

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Hum Gene Ther 2012;23:980-91

Safety And Tolerability Of Retinostat®, A Lentiviral-vector Based Gene Therapy Product For The Treatment Of Wet Age-related Macular Degeneration, In Rabbits And Monkeys

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Investigative Ophthalmology & Visual Science, 52(14), pp.488-488

Subretinal Administration of Fluorescent Microspheres in the Minipig

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Investigative Ophthalmology & Visual Science, 52(14), pp.1358-1358.

Evaluation of EIAV Based Lentiviral Vectors Following Ocular Delivery in the Nonhuman Primate Model: Development of RetinoStat®

Read more about Evaluation of EIAV Based Lentiviral Vectors Following Ocular Delivery in the Nonhuman Primate Model: Development of RetinoStat®

Investigative Ophthalmology & Visual Science, 49(13), pp.5340-5340